Raizada MK, Lu D, Iyer S, Katovich M
Losartan versus gene therapy: Chronic control of high blood pressure in spontaneously hypertensive rats
50th Annual Fall Conference AHA Council for High Blood Pressure Research
Hypertens (Sep) 28:535 1996

(also reviewed is the following related abstract from the same meeting: Prolonged reduction of high blood pressure with an in vivo nonpathogenic, adeno-associated viral vector delivery of AT1-R mRNA antisense. by M. I. Phillips, D. Mohuczy-Dominiack, S. Galli, T. Zelles, Univ. Florida. Hypertension 7: 535, 1996.)

Despite a rather large armamentarium of effective anti-hypertensive agents, the pharmacologic treatment for systemic hypertension is still fraught with difficulties. Patients must take life-long medication, often two, three or four time a day. In addition to problems with compliance, these therapies have significant side effects.

These two remarkable studies are the first reports of using gene therapy to treat hypertension in laboratory animals. Both studies use the spontaneously hypertensive rat (SHR) model of hypertension, which develop reproducible hypertension which is responsive to the angiotensin (AT-1) receptor antagonist Losartan. These abstracts from the same institution take two different approaches.

The first abstract uses a retrovirus containing the 'anti-sense' portion of the AT-1 receptor to inhibit expression of the AT-1 receptor. The virus was given once at 5 days of life to SHR and control (WKY) rats. This single injection decreased expression and function of the AT-1 receptor protein for 90 days. The lack of receptor function was documented by finding decreases in AT-1 stimulated thirst and pressor responses. Blood pressure was decreased by 30-40 mmHg at 90 days post treatment, with no changes in the control rats. Finally, treatment with Losartan failed to drop blood pressure, indicating that the genetic intervention had produced a maximal anti-hypertensive effect. Thus, a single intravenous injection produced long term 3 months control of hypertension. Imagine the possibilities .....

The second report uses a different viral vector injected into the brain, but also achieves prolonged (5 weeks) reduction in blood pressure. They injected an adeno-associated virus which also contained the anti-sense portion of the AT-1 receptor. This particular virus does not stimulate inflammation or an immune response, both of which limit the effectiveness and duration of biological effect. A single injection of the vector was given to adult SHR or WKY rats either into the hypothalamus or into the lateral ventricles. The blood pressure was reduced for up to 5 weeks post injection. While this approach is less clinically useful because of the hazards of the brain injections, it nevertheless indicated that a prolonged reduction in high blood pressure can be achieved with vectors delivering the antisense DNA to the AT1 receptors.

Comment: Obviously, more work needs to be performed to determine the optimal viral vector, site of injection, method of delivery, and target gene. However, these exciting results are but a mere glimpse of the future of medical practices. An exciting time we live in... (Robert A. Star, M.D., University of Texas Southwestern Medical Center)

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50th Annual Fall Conference AHA Council for High Blood Pressure Research
H: Pathophysiology : Genetics